The information you provide to the chat will be collected and recorded to improve your experience and for quality assurance. Please read our privacy policy to see how we are storing and protecting your data.
How can we help you today?
Search Patheon
Recent searches
Clear History
Suggestions
All Results
Recent searches
Clear History
Suggestions
All Results
Search
US | EN
Rising to the rare disease challenge: Key considerations in large-molecule orphan drug development
Whitepaper
Rare diseases present a unique set of challenges within drug development due to small-scale manufacturing, limited time/data, small sample sizes, and costs. Learn how to overcome these challenges with:
- Process design decisions for clinical batches across the three stages of validation
- Key formulation considerations for sterile dosage forms based on the physical, chemical, and biologic characteristics of the drug substances
- Optimal API quantities for preclinical development and phase I studies